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Rare Diseases
Latest News & Journal Articles View All
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    ASH 2024Iron Overload: What Hematologists Should Know -     
    
    
    
        Exclusive-US NIH Reverses Conference Travel Ban for Scientists
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        Why Listening to Patients Matters in Rare Disease Research -     
    
                
    
    AAN 2025Inebilizumab Effective Up to 52 Weeks in Myasthenia Gravis -     
    
                
    
    
        Biologics Outperform Conventional Therapy in Still’s Disease -     
    
                
    
    WCM-EADO 2025Melanoma’s Hidden Toll in Skin of Color -     
    
    
    
        Rhythm Pharma's Drug for Rare Obesity Meets Late-stage Trial Goal
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        US FDA Approves First Treatment for Rare Genetic Disorder Prader-Willi Syndrome